For the first time, a CRISPR-based therapy has been injected directly into a person’s body to treat a disease. Leber congenital amaurosis 10 (LCA10) is a genetic disease and a leading cause of childhood blindness. With CRISPR, doctors hope to fix the genetic mutation that causes LCA10 and restore vision.
Click below to hear the story from Madeline Sofia and Rob Stein on NPR’s daily science podcast, Short Wave, or download wherever you get your podcasts.
Yep. They Injected CRISPR Into An Eyeball
Short Wave | NPR | March 19, 2020